hereditary disease

There are already more than 7,000 hereditary diseases in the world.

"You see the same amyloid plaques in the hereditary disease," he said.

The recent approval of a CRISPR-Cas9 therapy for sickle cell disease demonstrates that gene editing tools can do a superb job knocking out genes to cure hereditary disease.

Although people of African ancestry are most frequently and severely affected by this hereditary disease, its genetic underpinnings in this population have rarely been studied.

Gene therapy currently represents the most promising approach for the treatment of hereditary diseases.